Edición del genoma: linfohistiocitosis, angioedema hereditario

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– Li X, Wirtz T, Weber T, Lebedin M, Lowenstein ED, Sommermann T, et al. Precise CRISPR-Cas9 gene repair in autologous memory T cells to treat familial hemophagocytic lymphohistiocytosis. Science Immunology, 2024;9(92).
– Longhurst HJ, Lindsay K, Petersen RS, Fijen LM, Gurugama P, Maag D, et al. CRISPR-Cas9 In Vivo Gene Editing of KLKB1 for Hereditary Angioedema. N Engl J Med 2024;390:432-441.

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